by Madaline Spencer | Aug 5, 2024
Stiff person syndrome (SPS) is a rare, progressive disease that affects the nervous system, specifically the brain and spinal cord. The syndrome affects twice as many women as men. SPS is caused by increased muscle activity due to decreased inhibition of the central...
by Madaline Spencer | Aug 3, 2024
The U.S. Food and Drug Administration (FDA) has approved Tecelra (afamitresgene autoleucel or afami-cel) for the treatment of unresectable or metastatic synovial sarcoma in adults with certain HLA types who have received prior chemotherapy. Synovial sarcoma is a rare...
by Madaline Spencer | Aug 2, 2024
John Carmichael, MD, Co-director of the USC Pituitary Center and Clinical Chief for the Division of Endocrinology, discusses an analysis of growth hormone replacement therapy in patients under the age of 60 years. Growth hormone deficiency (GHD) is a...
by Madaline Spencer | Jul 29, 2024
The U.S. Food and Drug Administration (FDA) has approved Brineura (cerliponase alfa) for the treatment of Neuronal ceroid lipofuscinosis 2 (CLN2) disease in children under three years of age. CLN2 disease is a rare disorder that affects the nervous...
by Madaline Spencer | Jul 29, 2024
Patty Ketting, Executive Director of the HypoPARAthyroidism Association and a patient with hypoparathyroidism, discusses challenges of hypoparathyroidism. Hypoparathyroidism is is a rare endocrine disorder in which the parathyroid glands in the neck do...