by Madaline Spencer | Dec 17, 2025
A recent study, published in the New England Journal of Medicine, looked at the effects of sotatercept for pulmonary arterial hypertension (PAH) within the first year after diagnosis. PAH affects the heart and lungs. It is characterized by abnormally high blood...
by Madaline Spencer | Dec 16, 2025
The U.S. Food and Drug Administration (FDA) has approved an oral pellet formulation of Orladeyo (berotralstat) for prophylactic therapy in pediatric patients with hereditary angioedema (HAE) ages 2 to less than 12 years of age. HAE is a condition characterized by...
by Madaline Spencer | Dec 16, 2025
Michael Manning, MD, Allergist and Immunologist, discusses long-term data with Dawnzera (donidalorsen) for the treatment of patients with hereditary angioedema (HAE). HAE is a condition where people have recurrent episodes of severe swelling of the skin...
by Madaline Spencer | Dec 15, 2025
A recent study, published in Nature Medicine, looked at the effects of vutrisiran on cardiac structure and function in patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM) through a secondary analysis of the HELIOS-B clinical trial. ATTR-CM is a rare...
by Madaline Spencer | Dec 12, 2025
The U.S. Food and Drug Administration (FDA) has approved Waskyra (etuvetidigene autotemcel) for the treatment of patients ages 6 months and older with Wiskott-Aldrich syndrome (WAS). WAS is a disease with immunological deficiency and reduced ability to form blood...
