by Madaline Spencer | Oct 28, 2025
Wildon Farwell, MD, Chief Medical Officer at Satellos, discusses the safety and efficacy of SAT-3247 to treat adults with Duchenne muscular dystrophy (DMD). DMD is a genetic neuromuscular disorder characterized by progressive muscle wasting. DMD occurs...
by Madaline Spencer and Scott Harwood | Oct 27, 2025
The U.S. Food and Drug Administration (FDA) has approved Blenrep (belantamab mafodotin) in combination with bortezomib and dexamethasone (BVd) for the treatment of adult patients with relapsed/refractory multiple myeloma (MM). The indication is for those who have...
by Madaline Spencer | Oct 24, 2025
Lawrence Lustig, MD, Professor at Columbia University Medical Center, discusses early results from the CHORD clinical trial testing gene therapy to treat otoferlin-related hearing loss. Otoferlin (OTOF)-related hearing loss is a rare genetic auditory...
by Madaline Spencer | Oct 23, 2025
The U.S. Food and Drug Administration (FDA) has approved Epioxa (riboflavin 5’-phosphate ophthalmic solution) for the treatment of patients with keratoconus. Keratoconus is a rare eye condition characterized by the progressive thinning and weakening of the cornea....
by Madaline Spencer | Oct 23, 2025
Tiffany Graham Charkosky, author and patient with Lynch syndrome, discusses her experience with genetic testing and her book LIVING PROOF: How Love Defied Genetic Legacy. Lynch syndrome is a rare inherited condition characterized by increased risk for...
