FDA Approves Garadacimab for Hereditary Angioedema

The U.S. Food and Drug Administration (FDA) has approved Andembry (garadacimab) for the treatment of hereditary angioedema (HAE) in patients ages 12 years and older.   Hereditary Angioedema HAE is a rare condition characterized by recurrent episodes of severe...

Evolving Policy Landscapes for Rare Disease Access

Deb Jennings, Head of North America Patient Services Operations at Kyowa Kirin, discusses evolving policy landscapes for rare disease access.     In a panel discussion at the 2025 World Orphan Drug Congress, Ms. Jennings explained the volatility of the...

Patient Experience With Stevens-Johnson Syndrome

Katie Niemeyer, patient advocate, discusses her experience with Stevens-Johnson syndrome/toxic epidermal necrolysis (SJS/TEN).     SJS/TEN is a very severe reaction that causes skin tissue to die and detach. SJS and TEN previously were thought to be separate...