by Madaline Spencer | Apr 1, 2025
The U.S. Food and Drug Administration (FDA) has approved Vykat XR (diazoxide choline), for the treatment of hyperphagia in patients four years of age and older with Prader-Willi syndrome (PWS). PWS is a rare genetic condition that affects many parts of the body but...
by Madaline Spencer | Mar 31, 2025
A recent study analyzed the incidence and characteristics of cutaneous squamous cell carcinoma (cSCC) in patients with Sézary syndrome. Sézary syndrome is a rare, aggressive form of cutaneous T-cell lymphoma (CTCL), a group of rare cancers that occur when T-cells...
by Madaline Spencer | Mar 28, 2025
The U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) for rivoceranib plus camrelizumab to treat unresectable hepatocellular carcinoma (HCC). HCC is a rare liver cancer characterized by nodules composed of neoplastic epithelial cells...
by Madaline Spencer | Mar 28, 2025
Generalized pustular psoriasis (GPP) is a rare, severe form of psoriasis characterized by sterile pustules across large areas of skin. The condition most commonly affects individuals between the ages of 40 and 59 years. GPP may occur alongside plaque psoriasis and...
by Madaline Spencer | Mar 27, 2025
A recent study illustrated clinical improvements in patients with retinal dystrophy treated with gene therapy. Retinal dystrophy is a rare ophthalmology condition caused by a genetic deficiency of AIPL1. The condition is characterized by severe and rapid progression...
