GRIDS Symposium Celebrates its 10th Anniversary

Ozlem Goker-Alpan, MD, Founder and Chief Medical Officer of the Lysosomal & Rare Disorders Research & Treatment Center (LDRTC), discusses her work in lysosomal storage diseases and the GRIDS conference.     Lysosomal diseases are a group of rare...

New Data on Investigational Dravet Syndrome Treatment

Joseph E. Sullivan, MD, Professor of Neurology & Pediatrics at University of California San Francisco and Director of Benioff Children’s Hospital Pediatric Epilepsy Center of Excellence, discusses zovrevunersen for the treatment of patients with Dravet syndrome....