New Data on Investigational Dravet Syndrome Treatment

by Madaline Spencer | Jan 6, 2025

Joseph E. Sullivan, MD, Professor of Neurology & Pediatrics at University of California San Francisco and Director of Benioff Children’s Hospital Pediatric Epilepsy Center of Excellence, discusses zovrevunersen for the treatment of patients with Dravet syndrome....

Citizen Health: AI-Powered Platform for Rare Conditions

by Madaline Spencer | Jan 3, 2025

Farid Vij and Nasha Fitter, co-founders of Citizen Health, discuss how their organization helps rare disease patients. Citizen Health was founded in 2023 as an AI-powered health platform for individuals managing rare and complex conditions. With a focus on...

Protected: Patient Experience Living with Chronic Cough

by Madaline Spencer | Jan 1, 2025

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by Madaline Spencer | Jan 1, 2025

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PFIC and Alagille Syndrome Studies

by Madaline Spencer | Dec 30, 2024

James Squires, MD, University of Pittsburgh, discusses recent data regarding Bylvay (odevixibat) in patients with progressive familial intrahepatic cholestasis (PFIC) and Alagille syndrome. PFIC is a heterogeneous group of autosomal recessive disorders of...

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New Data on Investigational Dravet Syndrome Treatment

Citizen Health: AI-Powered Platform for Rare Conditions

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PFIC and Alagille Syndrome Studies

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