by Madaline Spencer | Aug 15, 2024
Erdheim-Chester disease (ECD) is a rare condition affecting many parts of the body. Although diagnosed in some children, it most commonly affects adults. ECD causes the overproduction of histiocytes, which then accumulate in tissues and organs. Parts of the body that...
by Madaline Spencer | Aug 14, 2024
Maria Fleseriu, MD, Director of the Pituitary Center at Oregon Health and Science University, discusses a post hoc analysis of three phase 3 studies analyzing the use of oral octreotide in patients with acromegaly. Acromegaly is a hormonal disorder that...
by Madaline Spencer | Aug 13, 2024
James “Brad” Elder, MD, Director of Neurosurgical Oncology at the Ohio State University Comprehensive Cancer Center, discusses a clinical trial evaluating the investigational gene therapy, AVB-101 in patients with frontotemporal dementia (FTD). FTD is a...
by Madaline Spencer | Aug 12, 2024
Kelly Knupp, MD, Associate Professor of Pediatrics and Neurology at the University of Colorado, discusses supplemental data on the efficacy of fenfluramine in treating Dravet syndrome-associated seizures. Dravet syndrome is the most severe of a group of...
by Madaline Spencer | Aug 8, 2024
Pisit “Duke” Pitukcheewanont, MD, Chief Medical Officer for Lumos Pharma, discusses a phase 2 trial evaluating LUM-201 (ibutamoren) for treatment of growth hormone deficiency. Pediatric growth hormone deficiency (PGHD) is a rare condition characterized...