by Madaline Spencer | Oct 30, 2024
Real-world data on Orladeyo (berotralstat) was presented at the Annual Scientific Meeting of the American College of Allergy, Asthma & Immunology (ACAAI) in Boston. This new data provides insight on berotralstat’s effectiveness in managing hereditary angioedema...
by Madaline Spencer | Oct 29, 2024
Louie Lee, PhD, Neurological Physiotherapist at University College London, discusses self-management of neuromuscular disorders (NMDs). NMDs are often progressive, rare, incurable and limited treatment options. As Dr. Lee explains, these factors are...
by Madaline Spencer | Oct 28, 2024
Linda Lowes, PhD, Nationwide Children’s Hospital, Columbus, Ohio, discusses results from a study focusing on gross motor delay in boys with Duchenne muscular dystrophy (DMD). DMD affects the muscles, leading to muscle wasting that gets worse over time....
by Madaline Spencer | Oct 25, 2024
Cathy Turner, Project Manager for DMD Care UK at the John Walton Muscular Dystrophy Research Center at Newcastle University, discusses the TREAT-NMD Advisory Committee for Therapeutics (TACT). TACT was established in 2009 with the goal of providing...
by Madaline Spencer | Oct 24, 2024
Charlotte Handberg, PhD, Senior Researcher at the National Rehabilitation Center for Neuromuscular Diseases in Denmark, and Associate Professor at Aarhus University, discusses results from a survey of parents’ hopes, worries, and needs for their children with spinal...
