by Madaline Spencer | Oct 1, 2024
Paul Bolno, CEO, and Anne-Marie Li-Kwai-Cheung, Chief Development Officer, of Wave Life Sciences, discuss interim data from the ongoing FORWARD-53 clinical trial for Duchenne muscular dystrophy (DMD). DMD affects the muscles, leading to progressive...
by Madaline Spencer | Sep 30, 2024
Tiffany Chow, MD, Behavioral Neurologist, Vice President of Clinical Development at Alector, discusses a survey conducted to better understand caregivers’ experiences With frontotemporal dementia (FTD). FTDs are a group of neurodegenerative disorders...
by Madaline Spencer | Sep 26, 2024
Andrew Dauber, MD, Chief of Endocrinology at Children’s National Hospital, discusses data presented on the efficacy of vosoritide in genetic skeletal conditions. Disease Overview Achondroplasia is a rare skeletal disorder that prevents the changing of cartilage...
by Madaline Spencer | Sep 25, 2024
Shubh Goel, VP, Head of Immuno-Oncology and GI Tumors Franchise for US Oncology at AstraZeneca, discusses results from the HIMALAYA clinical trial for hepatocellular carcinoma (HCC). HCC is a rare liver carcinoma characterized by nodules occurring within...
by Madaline Spencer | Sep 24, 2024
Elizabeth Berry-Kravis, MD, PhD, Pediatric Neurologist at Rush University Medical Center, discusses the development of an investigational drug for Fragile X syndrome (FXS). FXS is a rare genetic condition involving mutations in part of the X chromosome....
