by Madaline Spencer | Jun 27, 2024
The U.S. Food and Drug Administration (FDA) has approved VYVGART Hytrulo (efgartigimod alfa and hyaluronidase-qvfc) for the treatment of adult patients with chronic inflammatory demyelinating polyneuropathy (CIDP). CIDP is a rare neurological disorder...
by Madaline Spencer | Jun 27, 2024
Elisabeth Kugler, PhD, founder of Zeeks, and a patient with a rare disease, discusses her scleroderma and Raynaud’s diagnosis. Scleroderma is a rare connective tissue autoimmune disease that causes inflammation and fibrosis in the skin and other areas of...
by Madaline Spencer | Jun 26, 2024
Alan Krasner, MD, Chief Endocrinologist at Crinetics Pharmaceuticals, discusses a series of trials testing the safety and efficacy of investigational drug paltusotine for the treatment of acromegaly. Acromegaly is a rare endocrine disorder resulting from...
by Madaline Spencer | Jun 25, 2024
Marie Abrego, a person with neuromyelitis optica spectrum disorder (NMOSD), and Wendy Erler, Vice President of Patient Experience at Alexion Pharmaceuticals Inc, discuss getting diagnosed with NMOSD and finding support. NMOSD is a rare autoimmune...
by Madaline Spencer | Jun 24, 2024
Greg Josephs, Myasthenia Gravis Foundation of America (MGFA) Volunteer Ambassador and patient with myasthenia gravis (MG), discusses living with a rare disease and valuable resources available to patients. MG is a rare chronic autoimmune neuromuscular...
