by Madaline Spencer | Aug 22, 2024
Ponni Subbiah, MD, Senior Vice President of Acadia, Global Head of Medical Affairs and Chief Medical Officer, discusses long-term data from clinical trial extension of trofinetide in patients with Rett syndrome. Rett syndrome is a neurodevelopmental...
by Madaline Spencer | Aug 21, 2024
Dana Rizk, MD, Professor of Medicine at the University of Alabama at Birmingham, discusses the U.S. Food and Drug Administration (FDA) accelerated approval of Fabhalta (iptacopan) for the reduction of proteinuria in adults with IgA nephropathy (IgAN). ...
by Madaline Spencer | Aug 20, 2024
Stephen Russell, MD, Professor of Ophthalmology and Visual Sciences and Dina J. Schrage Professor of Macular Degeneration Research at the University of Iowa Carver College of Medicine, discusses long-term data on Luxturna (voretigene neparvovec-rzyl) for retinal...
by Madaline Spencer | Aug 16, 2024
Alan Percy, MD, Professor of Pediatrics, Neurology, Neurobiology, Genetics, and Psychology at University of Alabama, Birmingham and lead author for the LILAC-1 and LILAC-2 studies, discusses long-term data from clinical trial extension of trofinetide in patients with...
by Madaline Spencer | Aug 15, 2024
Erdheim-Chester disease (ECD) is a rare condition affecting many parts of the body. Although diagnosed in some children, it most commonly affects adults. ECD causes the overproduction of histiocytes, which then accumulate in tissues and organs. Parts of the body that...
