by Madaline Spencer | May 14, 2024
Patricia Weltin, CEO of Beyond the Diagnosis, provides an overview of tethered spinal cord syndrome (TSCS). Tethered spinal cord syndrome is a progressive, nervous system disorder in which tissue attaches to the spinal cord. This limits movement and...
by Madaline Spencer | May 13, 2024
Aravindhan Veerapandiyan, MD, pediatric neurologist at Arkansas Children’s Hospital, discusses the AFFINITY clinical trial testing the safety and efficacy of RGX-202 for patients with Duchenne muscular dystrophy (DMD). DMD is a rare disease affecting the...
by Madaline Spencer | May 8, 2024
Alan Percy, MD, Pediatric Neurologist at University of Alabama at Birmingham, describes the history of Rett syndrome. Rett syndrome is a neurodevelopmental condition primarily affecting girls. Patients with the disease appear to have normal psychomotor...
by Madaline Spencer | May 6, 2024
Benjamin Barnes, MD, Augusta University, discusses how he approaches ALS patient conversations and an ongoing platform trial. Amyotrophic lateral sclerosis (ALS), also referred to as Lou Gehrig’s disease, is a motor neuron disease which leads to...
by Madaline Spencer | May 3, 2024
Sean Studer, MD, MSc, FCCP, Head of Medical Affairs at the US Pulmonary Hypertension Group, at Johnson & Johnson, discusses the changing treatment landscape of pulmonary arterial hypertension (PAH), including the approval of Opsynvi (macitentan plus tadalafil)....
